Thursday - April 25, 2024

Duchenne Muscular Dystrophy Clinical Trial Updates 2024 | FDA Approvals, Therapies in Focus | Vyondys 53 (Golodirsen), Emflaza, Exondys 51, Translarna, Amondys 45, Viltepso, PF-06939926, Vamorolone

Duchenne Muscular Dystrophy Pipeline Insight Several major pharma and biotech companies such as Sarepta Therapeutics, PTC Therapeutics, Nippon Shinyaku, Pfizer, Santhera Pharmaceuticals/ReveraGen BioPharma, Taiho Pharmaceutical, FibroGen, Capricor, Daiichi Sankyo, Italfarmaco, Antisense Therapeutics, Solid Biosciences, among others, are actively working in … Continue reading